Encoded secures $275m for Dravet syndrome gene therapy
Proceeds will go towards a pivotal trial of the candidate in paediatric patients.
Cytiva Navigating cell therapy WP 4
Typewriter raises $56m Series A to progress non-viral gene therapy platform
FDA places clinical hold on Regenxbio’s RGX-121 in MPS II trial
A strategic shift for gene therapies: manufacturing and market size take centre stage
FDA grants accelerated approval to Ultragenyx’s Genglycos gene therapy
Andelyn Biosciences to develop GM2 gangliosidosis therapy
Repligen’s deal for BioLife Solutions indicates shift to manufacturing integration
Investigational CRISPR therapy succeeds in patient with drug-resistant E. Coli
