The Mucopolysaccharidosis IV (MPS IV) (Morquio Syndrome ) drugs in development market research report provides comprehensive information on the therapeutics under development for Mucopolysaccharidosis IV (MPS IV) (Morquio Syndrome ), complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA), and molecule type. GlobalData’s report assesses key aspects of the companies and drugs in development for Mucopolysaccharidosis IV (MPS IV) (Morquio Syndrome ). Buy the report here.
The report also covers the descriptive pharmacological action of the therapeutics and the latest news and press releases. Additionally, the report provides an overview of the key players involved in therapeutic development for Mucopolysaccharidosis IV (MPS IV) (Morquio Syndrome ) and features dormant and discontinued products.
GlobalData tracks eight drugs in development for Mucopolysaccharidosis IV (MPS IV) (Morquio Syndrome ) by eight companies/universities/institutes. The top development phase for Mucopolysaccharidosis IV (MPS IV) (Morquio Syndrome ) is preclinical with four drugs in that stage. The Mucopolysaccharidosis IV (MPS IV) (Morquio Syndrome ) pipeline has seven drugs in development by companies and one by universities/ institutes. Some of the companies in the Mucopolysaccharidosis IV (MPS IV) (Morquio Syndrome ) pipeline products market are: MandalMed, Esteve Pharmaceuticals and BioStrategies LC.
The key targets in the Mucopolysaccharidosis IV (MPS IV) (Morquio Syndrome ) pipeline products market include N-Acetylgalactosamine 6 Sulfatase, and Beta Galactosidase.
The key mechanisms of action in the Mucopolysaccharidosis IV (MPS IV) (Morquio Syndrome ) pipeline product include N-Acetylgalactosamine 6 Sulfatase Activator with three drugs in Preclinical. The Mucopolysaccharidosis IV (MPS IV) (Morquio Syndrome ) pipeline products include two routes of administration with the top ROA being Intravenous and six key molecule types in the Mucopolysaccharidosis IV (MPS IV) (Morquio Syndrome ) pipeline products market including Gene Therapy, and Recombinant Enzyme.
Mucopolysaccharidosis IV (MPS IV) (Morquio Syndrome ) overview
Mucopolysaccharidosis type IV (MPS IV), also known as Morquio syndrome, is a progressive condition that mainly affects the skeleton. The symptoms vary among affected individuals. The signs and symptoms of MPS IV usually become apparent during early childhood. Affected individuals develop various skeletal abnormalities, including short stature and “knock knees”.
For a complete picture of Mucopolysaccharidosis IV (MPS IV) (Morquio Syndrome )’s pipeline drug market, buy the report here.
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