The Niemann-Pick Disease Type C drugs in development market research report provides comprehensive information on the therapeutics under development for Niemann-Pick Disease Type C, complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA), and molecule type. GlobalData’s report assesses key aspects of the companies and drugs in development for Niemann-Pick Disease Type C. Buy the report here.
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The report also covers the descriptive pharmacological action of the therapeutics and the latest news and press releases. Additionally, the report provides an overview of the key players involved in therapeutic development for Niemann-Pick Disease Type C and features dormant and discontinued products.
GlobalData tracks 26 drugs in development for Niemann-Pick Disease Type C by 23 companies/universities/institutes. The top development phase for Niemann-Pick Disease Type C is preclinical with 16 drugs in that stage. The Niemann-Pick Disease Type C pipeline has 21 drugs in development by companies and five by universities/ institutes. Some of the companies in the Niemann-Pick Disease Type C pipeline products market are: IntraBio, Scenic Biotech and Azafaros.
The key targets in the Niemann-Pick Disease Type C pipeline products market include NPC Intracellular Cholesterol Transporter 1, Ceramide Glucosyltransferase, and CD70 Antigen.
The key mechanisms of action in the Niemann-Pick Disease Type C pipeline product include NPC Intracellular Cholesterol Transporter 1 Activator with five drugs in Preclinical. The Niemann-Pick Disease Type C pipeline products include five routes of administration with the top ROA being Oral and five key molecule types in the Niemann-Pick Disease Type C pipeline products market including Small Molecule, and Gene Therapy.
Niemann-Pick Disease Type C overview
Niemann-Pick disease is one of a group of lysosomal storage diseases that affect metabolism and that are caused by genetic mutations. It involves the accumulation of sphingolipids in cells throughout the body, particularly reticuloendothelial cells (the mononuclear phagocyte system). Symptoms include enlarged liver, brain damage, difficulty walking and swallowing, increased sensitivity to touch, difficulty speaking, loss of muscle tone, and learning difficulties.
For a complete picture of Niemann-Pick Disease Type C’s pipeline drug market, buy the report here.
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GlobalData’s pipeline drugs offers detailed profiles of pharmaceutical drugs in all stages of pre-clinical and clinical development, from discovery through to pre-registration. Coverage is limited to novel human medicinal drugs and biosimilars seeking market approval proprietary and is one of two primary repositories of pharmaceutical drug information offered by GlobalData through its Pharmaceutical Intelligence Center.
